Cell reprogramming DTI IPSCs Skeletal muscle Effector T cells Diseases Clinical trials AICD Albumin gene targeting MRI Cellules souches musculaires Brain damage Antisense oligonucleotides FOXO3a Distal myopathy Clinical markers Dicer Brain development ALS G-Secretase Long-term handicap Brain ASOs Bone involvement 3xTgAD Mice Bone development Aav10 Clinical trial CRISPR/SaCas9 GABA Fetal growth restriction FGR Lentiviral vectors Coagulation factor IX Mecp2 MRNP assembly Functional outcomes Adult patients Prematurity Chondrocytes Genetical therapy Biological marker Disease modifiers Amyotrophie spinale AAV C9orf72 Brain imaging Extremely preterm infants Microglia CNS MND Neuromuscular disease Icv Adenosine Errance diagnotique Maternal malnutrition Bioinformatics Epigenetic changes Fabry disease lysosomal storage disorders adeno asociated virus-9 Adult SMA Brain MRI Maladie neuromusculaire Duchenne Muscular Dystrophy IUGR GeneRide Intra-uterine growth restriction ASO Amyotrophic Lateral Sclerosis Modèle murin Calcium handling Melatonin Disease heterogeneity Biomarkers Brain injury Gene transfer Mouse model DPRs ERK1/2 signaling Dilated cardiomyopathy Intra-CSF delivery Spinal muscular atrophy Cartilage and bone regeneration Cell stemness MUNIX Blood brain barrier Cofilin-1 Gene therapy Genetics Early-onset sepsis Longitudinal progression Glucocorticosteroid IRM LMNA Maternal behavior MiRNA Les paramètres respiratoires SMN Inflammation FTD Biomarker